A MULTICENTER STUDY TO EVALUATE THE SAFETY, TOLERABILITY, AND EFFICACY OF A SINGLE DOSE OF AUTOLOGOUS CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEATS GENE-EDITED CD34+ HUMAN HEMATOPOIETIC STEM AND PROGENITOR CELLS (EDIT 301) IN TRANSFUSION DEPENDENT BETA THALASSEMIA (TDT)

Registry ID

EDIT 301-BTHAL-001

Source registry

HEALTH_CANADA

Status

Ongoing

Study type

INTERVENTIONAL

Sponsor

EDITAS MEDICINE, INC.

Start date

2023-04-19

Last update

2022-04-06

Conditions

• TRANSFUSION DEPENDENT THALASSEMIA

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